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11 in total

1. A cell-penetrating helical polymer for siRNA delivery to mammalian cells.

Authors: Nathan P Gabrielson; Hua Lu; Lichen Yin; Kyung Hoon Kim; Jianjun Cheng
Journal: Mol Ther Date: 2012-05-29 Impact factor: 11.454

2. Transgene produces massive overexpression of human beta -glucuronidase in mice, lysosomal storage of enzyme, and strain-dependent tumors.

Authors: Carole Vogler; Nancy Galvin; Beth Levy; Jeffery Grubb; Jinxing Jiang; Xiao Yan Zhou; William S Sly
Journal: Proc Natl Acad Sci U S A Date: 2003-02-18 Impact factor: 11.205

3. Lentivirus-mediated gene transfer of uroporphyrinogen III synthase fully corrects the porphyric phenotype in human cells.

Authors: F Géronimi; E Richard; I Lamrissi-Garcia; M Lalanne; C Ged; I Redonnet-Vernhet; F Moreau-Gaudry; H de Verneuil
Journal: J Mol Med (Berl) Date: 2003-04-30 Impact factor: 4.599

4. A novel common gamma chain mutation in a Chinese family with X-linked severe combined immunodeficiency (X-SCID; T(-)NK(-)B(+)).

Authors: Weiping Tan; Sifei Yu; Jiaying Lei; Baojing Wu; Changyou Wu
Journal: Immunogenetics Date: 2015-09-26 Impact factor: 2.846

5. In vivo selection of MGMT(P140K) lentivirus-transduced human NOD/SCID repopulating cells without pretransplant irradiation conditioning.

Authors: Steven P Zielske; Jane S Reese; Karen T Lingas; Jon R Donze; Stanton L Gerson
Journal: J Clin Invest Date: 2003-11 Impact factor: 14.808

6. A versatile reducible polycation-based system for efficient delivery of a broad range of nucleic acids.

Authors: Martin L Read; Surjeet Singh; Zubair Ahmed; Mark Stevenson; Simon S Briggs; David Oupicky; Lee B Barrett; Rachel Spice; Mark Kendall; Martin Berry; Jon A Preece; Ann Logan; Leonard W Seymour
Journal: Nucleic Acids Res Date: 2005-05-24 Impact factor: 16.971

7. Relationships between the physicochemical properties of an amphiphilic triblock copolymers/DNA complexes and their intramuscular transfection efficiency.

Authors: Mahajoub Bello-Roufaï; Olivier Lambert; Bruno Pitard
Journal: Nucleic Acids Res Date: 2006-12-20 Impact factor: 16.971

Gene therapy for SCID--a complication after remarkable progress.