Literature DB >> 12382645

Hematopoietic progenitor cel harvest and functionality in Fanconi anemia patients.

Jérôme Larghero, Jean-Pierre Marolleau, Jean Soulier, Alain Filion, Vanderson Rocha, Marc Benbunan, Eliane Gluckman.   

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Year:  2002        PMID: 12382645     DOI: 10.1182/blood-2002-07-2069

Source DB:  PubMed          Journal:  Blood        ISSN: 0006-4971            Impact factor:   22.113


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  10 in total

1.  Cyclophosphamide promotes engraftment of gene-modified cells in a mouse model of Fanconi anemia without causing cytogenetic abnormalities.

Authors:  Jennifer E Adair; Xin Zhao; Sylvia Chien; Min Fang; Martin E Wohlfahrt; Grant D Trobridge; Jason A Taylor; Brian C Beard; Hans-Peter Kiem; Pamela S Becker
Journal:  J Mol Med (Berl)       Date:  2012-06-03       Impact factor: 4.599

2.  Measles virus envelope pseudotyped lentiviral vectors transduce quiescent human HSCs at an efficiency without precedent.

Authors:  Camille Lévy; Fouzia Amirache; Anais Girard-Gagnepain; Cecilia Frecha; Francisco J Roman-Rodríguez; Ornellie Bernadin; Caroline Costa; Didier Nègre; Alejandra Gutierrez-Guerrero; Lenard S Vranckx; Isabelle Clerc; Naomi Taylor; Lars Thielecke; Kerstin Cornils; Juan A Bueren; Paula Rio; Rik Gijsbers; François-Loïc Cosset; Els Verhoeyen
Journal:  Blood Adv       Date:  2017-10-24

Review 3.  Stem cell gene therapy for fanconi anemia: report from the 1st international Fanconi anemia gene therapy working group meeting.

Authors:  Jakub Tolar; Jennifer E Adair; Michael Antoniou; Cynthia C Bartholomae; Pamela S Becker; Bruce R Blazar; Juan Bueren; Thomas Carroll; Marina Cavazzana-Calvo; D Wade Clapp; Robert Dalgleish; Anne Galy; H Bobby Gaspar; Helmut Hanenberg; Christof Von Kalle; Hans-Peter Kiem; Dirk Lindeman; Luigi Naldini; Susana Navarro; Raffaele Renella; Paula Rio; Julián Sevilla; Manfred Schmidt; Els Verhoeyen; John E Wagner; David A Williams; Adrian J Thrasher
Journal:  Mol Ther       Date:  2011-05-03       Impact factor: 11.454

4.  FANCL ubiquitinates β-catenin and enhances its nuclear function.

Authors:  Kim-Hien T Dao; Michael D Rotelli; Curtis L Petersen; Stefanie Kaech; Whitney D Nelson; Jane E Yates; Amy E Hanlon Newell; Susan B Olson; Brian J Druker; Grover C Bagby
Journal:  Blood       Date:  2012-05-31       Impact factor: 22.113

5.  Fanca-/- hematopoietic stem cells demonstrate a mobilization defect which can be overcome by administration of the Rac inhibitor NSC23766.

Authors:  Michael D Milsom; Andrew W Lee; Yi Zheng; Jose A Cancelas
Journal:  Haematologica       Date:  2009-06-02       Impact factor: 9.941

6.  Lentiviral-mediated genetic correction of hematopoietic and mesenchymal progenitor cells from Fanconi anemia patients.

Authors:  Ariana Jacome; Susana Navarro; Paula Río; Rosa M Yañez; Africa González-Murillo; M Luz Lozano; Maria Luisa Lamana; Julian Sevilla; Teresa Olive; Cristina Diaz-Heredia; Isabel Badell; Jesus Estella; Luis Madero; Guillermo Guenechea; José Casado; Jose C Segovia; Juan A Bueren
Journal:  Mol Ther       Date:  2009-03-10       Impact factor: 11.454

7.  Disease-corrected haematopoietic progenitors from Fanconi anaemia induced pluripotent stem cells.

Authors:  Angel Raya; Ignasi Rodríguez-Pizà; Guillermo Guenechea; Rita Vassena; Susana Navarro; María José Barrero; Antonella Consiglio; Maria Castellà; Paula Río; Eduard Sleep; Federico González; Gustavo Tiscornia; Elena Garreta; Trond Aasen; Anna Veiga; Inder M Verma; Jordi Surrallés; Juan Bueren; Juan Carlos Izpisúa Belmonte
Journal:  Nature       Date:  2009-05-31       Impact factor: 49.962

8.  Targeted gene therapy and cell reprogramming in Fanconi anemia.

Authors:  Paula Rio; Rocio Baños; Angelo Lombardo; Oscar Quintana-Bustamante; Lara Alvarez; Zita Garate; Pietro Genovese; Elena Almarza; Antonio Valeri; Begoña Díez; Susana Navarro; Yaima Torres; Juan P Trujillo; Rodolfo Murillas; Jose C Segovia; Enrique Samper; Jordi Surralles; Philip D Gregory; Michael C Holmes; Luigi Naldini; Juan A Bueren
Journal:  EMBO Mol Med       Date:  2014-04-06       Impact factor: 12.137

9.  Novel lineage depletion preserves autologous blood stem cells for gene therapy of Fanconi anemia complementation group A.

Authors:  Jennifer E Adair; Devikha Chandrasekaran; Gabriella Sghia-Hughes; Kevin G Haworth; Ann E Woolfrey; Lauri M Burroughs; Grace Y Choi; Pamela S Becker; Hans-Peter Kiem
Journal:  Haematologica       Date:  2018-07-05       Impact factor: 9.941

10.  The PI3K/Akt1 pathway enhances steady-state levels of FANCL.

Authors:  Kim-Hien T Dao; Michael D Rotelli; Brieanna R Brown; Jane E Yates; Juha Rantala; Cristina Tognon; Jeffrey W Tyner; Brian J Druker; Grover C Bagby
Journal:  Mol Biol Cell       Date:  2013-06-19       Impact factor: 4.138

  10 in total

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