Literature DB >> 12161592

Cardiovascular manifestations in 75 patients with Williams syndrome.

M Eronen1, M Peippo, A Hiippala, M Raatikka, M Arvio, R Johansson, M Kähkönen.   

Abstract

OBJECTIVE: The prevalence and types of various cardiovascular diseases in different age groups as well as the outcomes of cardiac surgery and other interventions were assessed in a population of 75 Williams syndrome (WS) patients aged 4 months to 76 years (median 22.7 years). STUDY
DESIGN: The diagnosis of WS was in each case confirmed by the clinical phenotype and by a FISH test showing elastin hemizygosity. Clinical and operative data were collected from all hospitals where the patients had been treated.
RESULTS: Cardiovascular symptoms were evident in 35 of 75 (47%) WS children at birth. During follow up, 44 of 75 (53%) WS patients were found to have cardiovascular defects. Among them, the definitive diagnosis was made before 1 year of age in 23 (52%) infants, between 1 year and 15 years of age in 14 (32%) children, and older than 15 years of age in 7 (16%) adults. Multiple obstructive cardiovascular diseases were found in six infants. Supravalvular aortic stenosis (SVAS) was diagnosed in 32/44 (73%), pulmonary arterial stenosis (PAS) in 18/44 (41%), aortic or mitral valve defect in 5/44 (11 %) of cases, and tetralogy of Fallot in one (2%) case. Altogether, 17/44 (39 %) underwent surgery or intervention. Surgery was most frequently performed in the infant group (6% v 21% v 0%, p=0.004). After 1 year of age, seven patients underwent SVAS relief and two cases PAS relief. Postoperatively there was no mortality (median follow up time 6.9 years). Arterial hypertension was found in 55% of adults. In three adults, arterial vasculopathy was not diagnosed until necropsy.
CONCLUSIONS: Our data indicate the following in WS. Cardiac symptoms are common in neonates. Heart disease diagnosed in infancy frequently requires operation. After 1 year of age, PAS tends to improve and SVAS to progress. Life long cardiac follow up is necessary because of the risks of developing vasculopathy or arterial hypertension.

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Year:  2002        PMID: 12161592      PMCID: PMC1735199          DOI: 10.1136/jmg.39.8.554

Source DB:  PubMed          Journal:  J Med Genet        ISSN: 0022-2593            Impact factor:   6.318


  22 in total

1.  Supravalvar aortic stenosis: unexpected findings at surgery.

Authors:  C Grahame-Clarke; W B Pugsley; R H Swanton
Journal:  Heart       Date:  1998-06       Impact factor: 5.994

2.  Williams-Beuren syndrome. Long-term results of surgical treatments in six patients.

Authors:  G M Actis Dato; M La Torre; P Caimmi; A Actis Dato; P Centofanti; G M Ottino; M Di Summa
Journal:  J Cardiovasc Surg (Torino)       Date:  1997-04       Impact factor: 1.888

Review 3.  Sudden death in Williams syndrome: report of ten cases.

Authors:  L M Bird; G F Billman; R V Lacro; R L Spicer; L K Jariwala; H E Hoyme; R Zamora-Salinas; C Morris; D Viskochil; M J Frikke; M C Jones
Journal:  J Pediatr       Date:  1996-12       Impact factor: 4.406

4.  Progressive left main coronary artery obstruction leading to myocardial infarction in a child with Williams syndrome.

Authors:  D Bonnet; V Cormier; E Villain; P Bonhoeffer; J Kachaner
Journal:  Eur J Pediatr       Date:  1997-10       Impact factor: 3.183

5.  Elevated ambulatory blood pressure in 20 subjects with Williams syndrome.

Authors:  K Broder; E Reinhardt; J Ahern; R Lifton; W Tamborlane; B Pober
Journal:  Am J Med Genet       Date:  1999-04-23

6.  Deletions of the elastin gene at 7q11.23 occur in approximately 90% of patients with Williams syndrome.

Authors:  E Nickerson; F Greenberg; M T Keating; C McCaskill; L G Shaffer
Journal:  Am J Hum Genet       Date:  1995-05       Impact factor: 11.025

7.  Three decades of follow-up of aortic and pulmonary vascular lesions in the Williams-Beuren syndrome.

Authors:  A Wessel; R Pankau; D Kececioglu; W Ruschewski; J H Bürsch
Journal:  Am J Med Genet       Date:  1994-09-01

8.  Novel arterial pathology in mice and humans hemizygous for elastin.

Authors:  D Y Li; G Faury; D G Taylor; E C Davis; W A Boyle; R P Mecham; P Stenzel; B Boak; M T Keating
Journal:  J Clin Invest       Date:  1998-11-15       Impact factor: 14.808

9.  Supravalvular aortic stenosis associated with a deletion disrupting the elastin gene.

Authors:  A K Ewart; W Jin; D Atkinson; C A Morris; M T Keating
Journal:  J Clin Invest       Date:  1994-03       Impact factor: 14.808

10.  Genetic approaches to cardiovascular disease. Supravalvular aortic stenosis, Williams syndrome, and long-QT syndrome.

Authors:  M T Keating
Journal:  Circulation       Date:  1995-07-01       Impact factor: 29.690

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2.  Supravalvular aortic stenosis and total occlusion of the brachiocephalic trunk.

Authors:  A M van Oort; M Willemsen
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3.  A Novel Imaging Finding in Williams Syndrome: The Coral Sign.

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4.  Biliary hypoplasia in Williams syndrome.

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5.  Intervention and management of congenital left heart obstructive lesions.

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Review 6.  Genetic Basis for Congenital Heart Disease: Revisited: A Scientific Statement From the American Heart Association.

Authors:  Mary Ella Pierpont; Martina Brueckner; Wendy K Chung; Vidu Garg; Ronald V Lacro; Amy L McGuire; Seema Mital; James R Priest; William T Pu; Amy Roberts; Stephanie M Ware; Bruce D Gelb; Mark W Russell
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7.  Williams syndrome predisposes to vascular stiffness modified by antihypertensive use and copy number changes in NCF1.

Authors:  Beth A Kozel; Joshua R Danback; Jessica L Waxler; Russell H Knutsen; Lisa de Las Fuentes; Gyorgy S Reusz; Eva Kis; Ami B Bhatt; Barbara R Pober
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8.  Developmental adaptation of the mouse cardiovascular system to elastin haploinsufficiency.

Authors:  Gilles Faury; Mylène Pezet; Russell H Knutsen; Walter A Boyle; Scott P Heximer; Sean E McLean; Robert K Minkes; Kendall J Blumer; Attila Kovacs; Daniel P Kelly; Dean Y Li; Barry Starcher; Robert P Mecham
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9.  Sudden unexpected death in a toddler with Williams syndrome.

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Review 10.  Mechanisms and treatment of cardiovascular disease in Williams-Beuren syndrome.

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