Literature DB >> 11984564

Immune reconstitution in ADA-SCID after PBL gene therapy and discontinuation of enzyme replacement.

Alessandro Aiuti, Sergio Vai, Alessandra Mortellaro, Giulia Casorati, Francesca Ficara, Grazia Andolfi, Giuliana Ferrari, Antonella Tabucchi, Filippo Carlucci, Hans D Ochs, Luigi D Notarangelo, Maria Grazia Roncarolo, Claudio Bordignon.   

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Year:  2002        PMID： 11984564     DOI： 10.1038/nm0502-423

Source DB:  PubMed          Journal:  Nat Med        ISSN： 1078-8956            Impact factor:   53.440


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  52 in total

1.  Gene doping: Olympic genes for Olympic dreams.

Authors:  Lucy Battery; Andrew Solomon; David Gould
Journal:  J R Soc Med       Date:  2011-12       Impact factor: 5.344

Review 2.  Advances in the field of lentivector-based transduction of T and B lymphocytes for gene therapy.

Authors:  Cecilia Frecha; Camille Lévy; François-Loïc Cosset; Els Verhoeyen
Journal:  Mol Ther       Date:  2010-08-24       Impact factor: 11.454

3.  T cell therapies-are T memory stem cells the answer?

Authors:  Jacqueline K Flynn; Paul R Gorry
Journal:  Ann Transl Med       Date:  2015-10

4.  Gammaretrovirus-mediated correction of SCID-X1 is associated with skewed vector integration site distribution in vivo.

Authors:  Kerstin Schwarzwaelder; Steven J Howe; Manfred Schmidt; Martijn H Brugman; Annette Deichmann; Hanno Glimm; Sonja Schmidt; Claudia Prinz; Manuela Wissler; Douglas J S King; Fang Zhang; Kathryn L Parsley; Kimberly C Gilmour; Joanna Sinclair; Jinhua Bayford; Rachel Peraj; Karin Pike-Overzet; Frank J T Staal; Dick de Ridder; Christine Kinnon; Ulrich Abel; Gerard Wagemaker; H Bobby Gaspar; Adrian J Thrasher; Christof von Kalle
Journal:  J Clin Invest       Date:  2007-08       Impact factor: 14.808

5.  Gene therapy in sport.

Authors:  R J Trent; I E Alexander
Journal:  Br J Sports Med       Date:  2006-01       Impact factor: 13.800

Review 6.  Update on clinical gene therapy in childhood.

Authors:  Waseem Qasim; H Bobby Gaspar; Adrian J Thrasher
Journal:  Arch Dis Child       Date:  2007-11       Impact factor: 3.791

Review 7.  High-level secretion of growth hormone by retrovirally transduced primary human keratinocytes: prospects for an animal model of cutaneous gene therapy.

Authors:  Cibele Nunes Peroni; Cláudia Regina Cecchi; Renata Damiani; Carlos R J Soares; Maria Teresa C P Ribela; Rosângela do Rocio Arkaten; Paolo Bartolini
Journal:  Mol Biotechnol       Date:  2006-10       Impact factor: 2.695

Review 8.  Gene therapy for sickle cell disease: An update.

Authors:  Selami Demirci; Naoya Uchida; John F Tisdale
Journal:  Cytotherapy       Date:  2018-05-30       Impact factor: 5.414

Review 9.  Genotoxicity of retroviral hematopoietic stem cell gene therapy.

Authors:  Grant D Trobridge
Journal:  Expert Opin Biol Ther       Date:  2011-03-07       Impact factor: 4.388

10.  A novel mutation in the ADA gene causing severe combined immunodeficiency in an Arab patient: a case report.

Authors:  Ali Hellani; Nidal Almassri; Khaled K Abu-Amero
Journal:  J Med Case Rep       Date:  2009-04-01
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