Literature DB >> 11442517

Effects of imilglucerase withdrawal on an adult with Gaucher disease.

I V Schwartz, S Karam, P Ashton-Prolla, K Michelin, J Coelho, R F Pires, M L Pereira, R Giugliani.   

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Year:  2001        PMID: 11442517     DOI: 10.1046/j.1365-2141.2001.02821-13.x

Source DB:  PubMed          Journal:  Br J Haematol        ISSN: 0007-1048            Impact factor:   6.998


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  2 in total

1.  Did the temporary shortage in supply of imiglucerase have clinical consequences? Retrospective observational study on 34 italian Gaucher type I patients.

Authors:  Laura Deroma; Annalisa Sechi; Andrea Dardis; Daniela Macor; Giulia Liva; Giovanni Ciana; Bruno Bembi
Journal:  JIMD Rep       Date:  2012-07-01

2.  Treatment Efficiency in Gaucher Patients Can Reliably Be Monitored by Quantification of Lyso-Gb1 Concentrations in Dried Blood Spots.

Authors:  Claudia Cozma; Paskal Cullufi; Guido Kramp; Marina Hovakimyan; Virtut Velmishi; Agim Gjikopulli; Sonila Tomori; Steffen Fischer; Sebastian Oppermann; Ulrike Grittner; Peter Bauer; Christian Beetz; Arndt Rolfs
Journal:  Int J Mol Sci       Date:  2020-06-27       Impact factor: 5.923

  2 in total

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