Literature DB >> 11405816

A family with X-linked dystonia-deafness syndrome with a novel mutation of the DDP gene.

H Ujike1, Y Tanabe, Y Takehisa, T Hayabara, S Kuroda.   

Abstract

BACKGROUND: X-linked dystonia-deafness syndrome (DDS) is characterized by early-onset deafness followed by progressive dystonia in adulthood. Only 4 families with the syndrome have been reported, and all were white.
OBJECTIVE: To describe the first nonwhite family with X-linked DDS, involving 5 affected males in 4 generations.
RESULTS: Clinical features of the family members, who were Japanese, were mostly consistent with reports of DDS in whites except for a lack of visual disturbances. Whereas microdeletions in the deafness-dystonia peptide (DDP) gene were found in 2 white DDS families, our patients showed a novel mutation (arg80ter) in exon 2 of the DDP gene.
CONCLUSION: The existence of a DDS family of Japanese origin with a new kind of mutation in the DDP gene provides additional evidence that the DDP gene is a causative gene for X-linked DDS.

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Year:  2001        PMID: 11405816     DOI: 10.1001/archneur.58.6.1004

Source DB:  PubMed          Journal:  Arch Neurol        ISSN: 0003-9942


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