Literature DB >> 11369190

Primary beta-sarcoglycanopathy manifesting as recurrent exercise-induced myoglobinuria.

R Cagliani1, G P Comi, L Tancredi, M Sironi, F Fortunato, R Giorda, A Bardoni, M Moggio, A Prelle, N Bresolin, G Scarlato.   

Abstract

We report an unusual presentation of a primary beta-sarcoglycanopathy (LGMD type 2E). A 12- year-old boy came to our attention after six episodes of exercise-induced myoglobinuria. Electromyogram showed mild myopathic features of the proximal lower limb muscles. Electrocardiogram was normal. Neurological examination revealed normal muscle strength and reduced deep tendon reflexes. A muscle biopsy showed rare regenerating fibers; the immunohistochemistry was normal for dystrophin, while all the sarcoglycans were diffusely decreased. Western blot analysis showed a relevant decrease of all sarcoglycan proteins and a mild dystrophin reduction. beta-Sarcoglycan gene analysis demonstrated a compound heterozygous status for these mutations: a novel A-T base pair substitution at nucleotide 85 in exon 2, changing the codon Arg to a stop codon; a C-T base pair substitution at nucleotide 272 in exon 3 changing a Arg to a Cys residue. We consider that exercise-induced myoglobinuria may be the presenting sign of primary beta-sarcoglycanopathy.

Entities:  

Mesh:

Substances:

Year:  2001        PMID: 11369190     DOI: 10.1016/s0960-8966(00)00207-8

Source DB:  PubMed          Journal:  Neuromuscul Disord        ISSN: 0960-8966            Impact factor:   4.296


  9 in total

Review 1.  Metabolic Myoglobinuria.

Authors:  Emanuele Barca; Valentina Emmanuele; Salvatore Billi DiMauro
Journal:  Curr Neurol Neurosci Rep       Date:  2015-10       Impact factor: 5.081

2.  Gene Delivery for Limb-Girdle Muscular Dystrophy Type 2D by Isolated Limb Infusion.

Authors:  Jerry R Mendell; Louis G Chicoine; Samiah A Al-Zaidy; Zarife Sahenk; Kelly Lehman; Linda Lowes; Natalie Miller; Lindsay Alfano; Beverly Galliers; Sarah Lewis; Darren Murrey; Ellyn Peterson; Danielle A Griffin; Kathleen Church; Sharon Cheatham; John Cheatham; Mark J Hogan; Louise R Rodino-Klapac
Journal:  Hum Gene Ther       Date:  2019-04-19       Impact factor: 5.695

3.  Beta-sarcoglycanopathy.

Authors:  Seema Kapoor; Medha Tatke; Sandeep Aggarwal; Ashish Gupta
Journal:  Indian J Pediatr       Date:  2005-01       Impact factor: 1.967

4.  Diagnostic evaluation of rhabdomyolysis.

Authors:  Jessica R Nance; Andrew L Mammen
Journal:  Muscle Nerve       Date:  2015-03-14       Impact factor: 3.217

5.  Mutations in GMPPB Presenting with Pseudometabolic Myopathy.

Authors:  Chiara Panicucci; Chiara Fiorillo; Francesca Moro; Guja Astrea; Giacomo Brisca; Federica Trucco; Marina Pedemonte; Paola Lanteri; Lucia Sciarretta; Carlo Minetti; Filippo M Santorelli; Claudio Bruno
Journal:  JIMD Rep       Date:  2017-04-30

6.  Myoglobinuria as first clinical sign of a primary alpha-sarcoglycanopathy.

Authors:  Ferdinando Ceravolo; Sonia Messina; Carmelo Rodolico; Pietro Strisciuglio; Daniela Concolino
Journal:  Eur J Pediatr       Date:  2013-08-30       Impact factor: 3.183

Review 7.  Therapeutic possibilities in the autosomal recessive limb-girdle muscular dystrophies.

Authors:  Volker Straub; Kate Bushby
Journal:  Neurotherapeutics       Date:  2008-10       Impact factor: 7.620

Review 8.  Rhabdomyolysis: a genetic perspective.

Authors:  Renata Siciliani Scalco; Alice R Gardiner; Robert Ds Pitceathly; Edmar Zanoteli; Jefferson Becker; Janice L Holton; Henry Houlden; Heinz Jungbluth; Ros Quinlivan
Journal:  Orphanet J Rare Dis       Date:  2015-05-02       Impact factor: 4.123

9.  Progression to Loss of Ambulation Among Patients with Autosomal Recessive Limb-girdle Muscular Dystrophy: A Systematic Review.

Authors:  Ivana F Audhya; Antoinette Cheung; Shelagh M Szabo; Emma Flint; Conrad C Weihl; Katherine L Gooch
Journal:  J Neuromuscul Dis       Date:  2022
  9 in total

北京卡尤迪生物科技股份有限公司 © 2022-2023.