Literature DB >> 11257473

Longitudinal data analysis: an application to construction of a natural history profile of Duchenne muscular dystrophy.

S A Hyde1, B F Steffensen, I Fløytrup, S Glent, A K Kroksmark, B Salling, U Werlauff, M Erlandsen.   

Abstract

A 30-month prospective study of 27 Scandinavian boys with confirmed diagnosis of Duchenne muscular dystrophy was carried out to construct profiles of the natural history of the disease. Assessments which included measures of voluntary muscle strength and function were done at 3 monthly intervals except for the first and second which were separated by 1 month. Recently developed statistical methods for analysis of longitudinal data with repeated observations on the same individual were used avoiding the problem of induced serial correlations. This allowed for the construction of both reference and prediction profiles for the variables %MRC, motor ability, walking time for 10 m and the sum of myometry of seven muscle groups.

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Year:  2001        PMID: 11257473     DOI: 10.1016/s0960-8966(00)00175-9

Source DB:  PubMed          Journal:  Neuromuscul Disord        ISSN: 0960-8966            Impact factor:   4.296


  7 in total

Review 1.  Systemic AAV Micro-dystrophin Gene Therapy for Duchenne Muscular Dystrophy.

Authors:  Dongsheng Duan
Journal:  Mol Ther       Date:  2018-07-17       Impact factor: 11.454

2.  Quadriceps muscle strength in Duchenne muscular dystrophy and effect of corticosteroid treatment.

Authors:  Luciano Merlini; Ilaria Cecconi; Antonia Parmeggiani; Duccio Maria Cordelli; Ada Dormi
Journal:  Acta Myol       Date:  2020-12-01

3.  Improvement of survival in Duchenne Muscular Dystrophy: retrospective analysis of 835 patients.

Authors:  Luigia Passamano; Antonella Taglia; Alberto Palladino; Emanuela Viggiano; Paola D'Ambrosio; Marianna Scutifero; Maria Rosaria Cecio; Vito Torre; Francesco DE Luca; Esther Picillo; Orlando Paciello; Giulio Piluso; Gerardo Nigro; Luisa Politano
Journal:  Acta Myol       Date:  2012-10

4.  Correlation of circulating CD133+ progenitor subclasses with a mild phenotype in Duchenne muscular dystrophy patients.

Authors:  Chiara Marchesi; Marzia Belicchi; Mirella Meregalli; Andrea Farini; Alessandra Cattaneo; Daniele Parolini; Manuela Gavina; Laura Porretti; Maria Grazia D'Angelo; Nereo Bresolin; Giulio Cossu; Yvan Torrente
Journal:  PLoS One       Date:  2008-05-21       Impact factor: 3.240

5.  The 6-minute walk test and other clinical endpoints in duchenne muscular dystrophy: reliability, concurrent validity, and minimal clinically important differences from a multicenter study.

Authors:  Craig M McDonald; Erik K Henricson; R Ted Abresch; Julaine Florence; Michelle Eagle; Eduard Gappmaier; Allan M Glanzman; Robert Spiegel; Jay Barth; Gary Elfring; Allen Reha; Stuart W Peltz
Journal:  Muscle Nerve       Date:  2013-07-17       Impact factor: 3.217

6.  The 6-minute walk test and other endpoints in Duchenne muscular dystrophy: longitudinal natural history observations over 48 weeks from a multicenter study.

Authors:  Craig M McDonald; Erik K Henricson; R Ted Abresch; Julaine M Florence; Michelle Eagle; Eduard Gappmaier; Allan M Glanzman; Robert Spiegel; Jay Barth; Gary Elfring; Allen Reha; Stuart Peltz
Journal:  Muscle Nerve       Date:  2013-06-26       Impact factor: 3.217

7.  Can Quantitative Muscle Strength and Functional Motor Ability Differentiate the Influence of Age and Corticosteroids in Ambulatory Boys with Duchenne Muscular Dystrophy?

Authors:  Cathleen Buckon; Susan Sienko; Anita Bagley; Mitell Sison-Williamson; Eileen Fowler; Loretta Staudt; Kent Heberer; Craig M McDonald; Michael Sussman
Journal:  PLoS Curr       Date:  2016-07-08
  7 in total

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