Literature DB >> 10906169

Gene therapy for lysosomal storage disorders with neuropathology.

Yiannis A Ioannou1.   

Abstract

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Year:  2000        PMID： 10906169     DOI： 10.1681/ASN.V1181542

Source DB:  PubMed          Journal:  J Am Soc Nephrol        ISSN： 1046-6673            Impact factor:   10.121


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  6 in total

Review 1.  Gene therapy for Fabry disease.

Authors:  C Siatskas; J A Medin
Journal:  J Inherit Metab Dis       Date:  2001       Impact factor: 4.982

Review 2.  Gene therapy for lysosomal storage diseases (LSDs) in large animal models.

Authors:  Mark Haskins
Journal:  ILAR J       Date:  2009

3.  Lysosomal enzyme replacement of the brain with intravenous non-viral gene transfer.

Authors:  Yun Zhang; Yuntao Wang; Ruben J Boado; William M Pardridge
Journal:  Pharm Res       Date:  2007-06-30       Impact factor: 4.200

4.  Restoration of the GM2 ganglioside metabolism in bone marrow-derived stromal cells from Tay-Sachs disease animal model.

Authors:  S Martino; C Cavalieri; C Emiliani; D Dolcetta; M G Cusella De Angelis; V Chigorno; G M Severini; K Sandhoff; C Bordignon; S Sonnino; A Orlacchio
Journal:  Neurochem Res       Date:  2002-08       Impact factor: 3.996

Review 5.  Brain Delivery of Nanomedicines: Trojan Horse Liposomes for Plasmid DNA Gene Therapy of the Brain.

Authors:  William M Pardridge
Journal:  Front Med Technol       Date:  2020-11-16

6.  The Trojan Horse Liposome Technology for Nonviral Gene Transfer across the Blood-Brain Barrier.

Authors:  Ruben J Boado; William M Pardridge
Journal:  J Drug Deliv       Date:  2011-11-16
  6 in total

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