Literature DB >> 10805762

Gene therapy for the hemoglobin disorders: past, present, and future.

D A Persons1, A W Nienhuis.   

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Year:  2000        PMID： 10805762      PMCID： PMC33980          DOI： 10.1073/pnas.97.10.5022

Source DB:  PubMed          Journal:  Proc Natl Acad Sci U S A        ISSN： 0027-8424            Impact factor:   11.205


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  38 in total

1.  Long-term expression of human adenosine deaminase in rhesus monkeys transplanted with retrovirus-infected bone-marrow cells.

Authors:  V W van Beusechem; A Kukler; P J Heidt; D Valerio
Journal:  Proc Natl Acad Sci U S A       Date:  1992-08-15       Impact factor: 11.205

2.  Sustained high-level reconstitution of the hematopoietic system by preselected hematopoietic cells expressing a transduced cell-surface antigen.

Authors:  R Pawliuk; C J Eaves; R K Humphries
Journal:  Hum Gene Ther       Date:  1997-09-01       Impact factor: 5.695

3.  Knockout-transgenic mouse model of sickle cell disease.

Authors:  T M Ryan; D J Ciavatta; T M Townes
Journal:  Science       Date:  1997-10-31       Impact factor: 47.728

4.  Long-term transfer and expression of the human beta-globin gene in a mouse transplant model.

Authors:  H Raftopoulos; M Ward; P Leboulch; A Bank
Journal:  Blood       Date:  1997-11-01       Impact factor: 22.113

5.  A globin enhancer acts by increasing the proportion of erythrocytes expressing a linked transgene.

Authors:  H G Sutherland; D I Martin; E Whitelaw
Journal:  Mol Cell Biol       Date:  1997-03       Impact factor: 4.272

6.  A proliferation switch for genetically modified cells.

Authors:  C A Blau; K R Peterson; J G Drachman; D M Spencer
Journal:  Proc Natl Acad Sci U S A       Date:  1997-04-01       Impact factor: 11.205

7.  Selection for G156A O6-methylguanine DNA methyltransferase gene-transduced hematopoietic progenitors and protection from lethality in mice treated with O6-benzylguanine and 1,3-bis(2-chloroethyl)-1-nitrosourea.

Authors:  B M Davis; J S Reese; O N Koç; K Lee; J E Schupp; S L Gerson
Journal:  Cancer Res       Date:  1997-11-15       Impact factor: 12.701

8.  The human beta-globin locus activation region alters the developmental fate of a human fetal globin gene in transgenic mice.

Authors:  T Enver; A J Ebens; W C Forrester; G Stamatoyannopoulos
Journal:  Proc Natl Acad Sci U S A       Date:  1989-09       Impact factor: 11.205

9.  The level of mRNA encoding the amphotropic retrovirus receptor in mouse and human hematopoietic stem cells is low and correlates with the efficiency of retrovirus transduction.

Authors:  D Orlic; L J Girard; C T Jordan; S M Anderson; A P Cline; D M Bodine
Journal:  Proc Natl Acad Sci U S A       Date:  1996-10-01       Impact factor: 11.205

10.  A majority of mice show long-term expression of a human beta-globin gene after retrovirus transfer into hematopoietic stem cells.

Authors:  M A Bender; R E Gelinas; A D Miller
Journal:  Mol Cell Biol       Date:  1989-04       Impact factor: 4.272
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  4 in total

1.  Loss of T cell-mediated antitumor immunity after construct-specific downregulation of retrovirally encoded T-cell receptor expression in vivo.

Authors:  M P Rubinstein; M L Salem; A N Kadima; C L Nguyen; W E Gillanders; M I Nishimura; D J Cole
Journal:  Cancer Gene Ther       Date:  2008-08-08       Impact factor: 5.987

2.  Transient in vivo beta-globin production after lentiviral gene transfer to hematopoietic stem cells in the nonhuman primate.

Authors:  Jun Hayakawa; Takahiro Ueda; Leszek Lisowski; Matthew M Hsieh; Kareem Washington; Oswald Phang; Mark Metzger; Allen Krouse; Robert E Donahue; Michel Sadelain; John F Tisdale
Journal:  Hum Gene Ther       Date:  2009-06       Impact factor: 5.695

3.  Sustained high-level polyclonal hematopoietic marking and transgene expression 4 years after autologous transplantation of rhesus macaques with SIV lentiviral vector-transduced CD34+ cells.

Authors:  Yoo-Jin Kim; Yoon-Sang Kim; Andre Larochelle; Gabriel Renaud; Tyra G Wolfsberg; Rima Adler; Robert E Donahue; Peiman Hematti; Bum-Kee Hong; Jean Roayaei; Keiko Akagi; Janice M Riberdy; Arthur W Nienhuis; Cynthia E Dunbar; Derek A Persons
Journal:  Blood       Date:  2009-04-01       Impact factor: 22.113

Review 4.  Genomic editing tools to model human diseases with isogenic pluripotent stem cells.

Authors:  Huen Suk Kim; Jeffrey M Bernitz; Dung-Fang Lee; Ihor R Lemischka
Journal:  Stem Cells Dev       Date:  2014-10-07       Impact factor: 3.272
  4 in total

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