Literature DB >> 10757357

Phase I clinical trial utilizing gene therapy for limb girdle muscular dystrophy: alpha-, beta-, gamma-, or delta-sarcoglycan gene delivered with intramuscular instillations of adeno-associated vectors.

H Stedman1, J M Wilson, R Finke, A L Kleckner, J Mendell.   

Abstract

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Year:  2000        PMID： 10757357     DOI： 10.1089/10430340050015671

Source DB:  PubMed          Journal:  Hum Gene Ther        ISSN： 1043-0342            Impact factor:   5.695


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  19 in total

1.  Proteolytic mapping of the adeno-associated virus capsid.

Authors:  Kim Van Vliet; Veronique Blouin; Mavis Agbandje-McKenna; Richard O Snyder
Journal:  Mol Ther       Date:  2006-09-27       Impact factor: 11.454

Review 2.  Challenges for gene therapy for muscular dystrophy.

Authors:  Jerry R Mendell; K Reed Clark
Journal:  Curr Neurol Neurosci Rep       Date:  2006-01       Impact factor: 5.081

3.  Good manufacturing practice production of self-complementary serotype 8 adeno-associated viral vector for a hemophilia B clinical trial.

Authors:  James A Allay; Susan Sleep; Scott Long; David M Tillman; Rob Clark; Gael Carney; Paolo Fagone; Jenny H McIntosh; Arthur W Nienhuis; Andrew M Davidoff; Amit C Nathwani; John T Gray
Journal:  Hum Gene Ther       Date:  2011-05       Impact factor: 5.695

Review 4.  Gene transfer to the vasculature: historical perspective and implication for future research objectives.

Authors:  Sarah J George; Andrew H Baker
Journal:  Mol Biotechnol       Date:  2002-10       Impact factor: 2.695

Review 5.  Evolving lessons on nanomaterial-coated viral vectors for local and systemic gene therapy.

Authors:  Dayananda Kasala; A-Rum Yoon; Jinwoo Hong; Sung Wan Kim; Chae-Ok Yun
Journal:  Nanomedicine (Lond)       Date:  2016-06-27       Impact factor: 5.307

6.  A novel gene expression control system and its use in stable, high-titer 293 cell-based adeno-associated virus packaging cell lines.

Authors:  Chunping Qiao; Bing Wang; Xiaodong Zhu; Juan Li; Xiao Xiao
Journal:  J Virol       Date:  2002-12       Impact factor: 5.103

7.  Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy.

Authors:  Yongping Yue; Ibrahim M Binalsheikh; Stacey B Leach; Timothy L Domeier; Dongsheng Duan
Journal:  Expert Opin Orphan Drugs       Date:  2015-12-17       Impact factor: 0.694

8.  Enhancing transduction of the liver by adeno-associated viral vectors.

Authors:  A C Nathwani; M Cochrane; J McIntosh; C Y C Ng; J Zhou; J T Gray; A M Davidoff
Journal:  Gene Ther       Date:  2008-08-14       Impact factor: 5.250

9.  Safety and efficacy of factor IX gene transfer to skeletal muscle in murine and canine hemophilia B models by adeno-associated viral vector serotype 1.

Authors:  Valder R Arruda; Joerg Schuettrumpf; Roland W Herzog; Timothy C Nichols; Nancy Robinson; Yasmin Lotfi; Federico Mingozzi; Weidong Xiao; Linda B Couto; Katherine A High
Journal:  Blood       Date:  2003-09-11       Impact factor: 22.113

10.  The TLR9-MyD88 pathway is critical for adaptive immune responses to adeno-associated virus gene therapy vectors in mice.

Authors:  Jiangao Zhu; Xiaopei Huang; Yiping Yang
Journal:  J Clin Invest       Date:  2009-07-01       Impact factor: 14.808
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