Literature DB >> 10468539

Gene therapy for the hemophilias.

M A Kay, K High.   

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Year:  1999        PMID： 10468539      PMCID： PMC33717          DOI： 10.1073/pnas.96.18.9973

Source DB:  PubMed          Journal:  Proc Natl Acad Sci U S A        ISSN： 0027-8424            Impact factor:   11.205


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  40 in total

1.  Genetic induction of immune tolerance to human clotting factor VIII in a mouse model for hemophilia A.

Authors:  G L Evans; R A Morgan
Journal:  Proc Natl Acad Sci U S A       Date:  1998-05-12       Impact factor: 11.205

2.  Sustained correction of bleeding disorder in hemophilia B mice by gene therapy.

Authors:  L Wang; K Takabe; S M Bidlingmaier; C R Ill; I M Verma
Journal:  Proc Natl Acad Sci U S A       Date:  1999-03-30       Impact factor: 11.205

3.  Hepatocyte growth factor induces hepatocyte proliferation in vivo and allows for efficient retroviral-mediated gene transfer in mice.

Authors:  G A Patijn; A Lieber; D B Schowalter; R Schwall; M A Kay
Journal:  Hepatology       Date:  1998-09       Impact factor: 17.425

4.  A coagulation factor IX-deficient mouse model for human hemophilia B.

Authors:  H F Lin; N Maeda; O Smithies; D L Straight; D W Stafford
Journal:  Blood       Date:  1997-11-15       Impact factor: 22.113

5.  Correction of hemophilia B in canine and murine models using recombinant adeno-associated viral vectors.

Authors:  R O Snyder; C Miao; L Meuse; J Tubb; B A Donahue; H F Lin; D W Stafford; S Patel; A R Thompson; T Nichols; M S Read; D A Bellinger; K M Brinkhous; M A Kay
Journal:  Nat Med       Date:  1999-01       Impact factor: 53.440

6.  Long-term correction of canine hemophilia B by gene transfer of blood coagulation factor IX mediated by adeno-associated viral vector.

Authors:  R W Herzog; E Y Yang; L B Couto; J N Hagstrom; D Elwell; P A Fields; M Burton; D A Bellinger; M S Read; K M Brinkhous; G M Podsakoff; T C Nichols; G J Kurtzman; K A High
Journal:  Nat Med       Date:  1999-01       Impact factor: 53.440

7.  Adeno-associated viral vector-mediated gene transfer of human blood coagulation factor IX into mouse liver.

Authors:  H Nakai; R W Herzog; J N Hagstrom; J Walter; S H Kung; E Y Yang; S J Tai; Y Iwaki; G J Kurtzman; K J Fisher; P Colosi; L B Couto; K A High
Journal:  Blood       Date:  1998-06-15       Impact factor: 22.113

8.  Expression of human factor IX in rat capillary endothelial cells: toward somatic gene therapy for hemophilia B.

Authors:  S N Yao; J M Wilson; E G Nabel; S Kurachi; H L Hachiya; K Kurachi
Journal:  Proc Natl Acad Sci U S A       Date:  1991-09-15       Impact factor: 11.205

9.  Haemophilia B mutations in a complete Swedish population sample: a test of new strategy for the genetic counselling of diseases with high mutational heterogeneity.

Authors:  P M Green; A J Montandon; R Ljung; D R Bentley; I M Nilsson; S Kling; F Giannelli
Journal:  Br J Haematol       Date:  1991-07       Impact factor: 6.998

10.  Targeted inactivation of the coagulation factor IX gene causes hemophilia B in mice.

Authors:  R K Kundu; F Sangiorgi; L Y Wu; K Kurachi; W F Anderson; R Maxson; E M Gordon
Journal:  Blood       Date:  1998-07-01       Impact factor: 22.113
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  19 in total

1.  Kinetics of liver repopulation after bone marrow transplantation.

Authors:  Xin Wang; Eugenio Montini; Muhsen Al-Dhalimy; Eric Lagasse; Milton Finegold; Markus Grompe
Journal:  Am J Pathol       Date:  2002-08       Impact factor: 4.307

2.  In vivo selection of transplanted hepatocytes by pharmacological inhibition of fumarylacetoacetate hydrolase in wild-type mice.

Authors:  Nicole K Paulk; Karsten Wursthorn; Annelise Haft; Carl Pelz; Gregory Clarke; Amy H Newell; Susan B Olson; Cary O Harding; Milton J Finegold; Raymond L Bateman; John F Witte; Ronald McClard; Markus Grompe
Journal:  Mol Ther       Date:  2012-08-07       Impact factor: 11.454

3.  Efficacy of engineered FVIII-producing skeletal muscle enhanced by growth factor-releasing co-axial electrospun fibers.

Authors:  I-Chien Liao; Kam W Leong
Journal:  Biomaterials       Date:  2010-11-16       Impact factor: 12.479

4.  Efficient AAV1-AAV2 hybrid vector for gene therapy of hemophilia.

Authors:  Bernd Hauck; Ray Ruian Xu; Jing Xie; Wenman Wu; Qiulan Ding; Matthew Sipler; Hongli Wang; Ling Chen; J Fraser Wright; Weidong Xiao
Journal:  Hum Gene Ther       Date:  2006-01       Impact factor: 5.695

5.  AAV-mediated gene targeting is significantly enhanced by transient inhibition of nonhomologous end joining or the proteasome in vivo.

Authors:  Nicole K Paulk; Laura Marquez Loza; Milton J Finegold; Markus Grompe
Journal:  Hum Gene Ther       Date:  2012-06-25       Impact factor: 5.695

6.  In vivo gene transfer strategies to achieve partial correction of von Willebrand disease.

Authors:  Lan Wang; Jonathan B Rosenberg; Bishnu P De; Barbara Ferris; Rui Wang; Stefano Rivella; Stephen M Kaminsky; Ronald G Crystal
Journal:  Hum Gene Ther       Date:  2012-06-25       Impact factor: 5.695

7.  Prospects for the use of artificial chromosomes and minichromosome-like episomes in gene therapy.

Authors:  Sara Pérez-Luz; Javier Díaz-Nido
Journal:  J Biomed Biotechnol       Date:  2010-08-24

8.  Complete correction of hemophilia A with adeno-associated viral vectors containing a full-size expression cassette.

Authors:  Hui Lu; Lingxia Chen; Jinhui Wang; Bernd Huack; Rita Sarkar; Shangzhen Zhou; Ray Xu; Qiulan Ding; Xuefeng Wang; Hongli Wang; Weidong Xiao
Journal:  Hum Gene Ther       Date:  2008-06       Impact factor: 5.695

9.  The enhancing effects of the light chain on heavy chain secretion in split delivery of factor VIII gene.

Authors:  Lingxia Chen; Fuxiang Zhu; Juan Li; Hui Lu; Haiyan Jiang; Rita Sarkar; Valder R Arruda; Jinhui Wang; Jennifer Zhao; Glenn F Pierce; Qiulan Ding; Xuefeng Wang; Hongli Wang; Steven W Pipe; Xiang-Qin Liu; Xiao Xiao; Rodney M Camire; Weidong Xiao
Journal:  Mol Ther       Date:  2007-07-24       Impact factor: 11.454

10.  Treatment of Hemophilia A in Utero and Postnatally using Sheep as a Model for Cell and Gene Delivery.

Authors:  Christopher D Porada; Graça Almeida-Porada
Journal:  J Genet Syndr Gene Ther       Date:  2012-05-25
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